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Experimental Gene Therapy Slows Huntington's Disease By 75%

Experimental Gene Therapy Slows Huntington's Disease By 75%

Experimental Gene Therapy Slows Huntington's Disease By 75%
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The Spin

ThisWhile ispromising, thethis firstexpensive successful treatment torequiring slowcomplex the18-hour progressionbrain ofsurgery Huntington'swill diseaseremain afterinaccessible decadesto ofmost failedpatients attemptswho desperately need it. The 75%results reductionare inbased diseaseon advancementonly means29 patients canwithout maintainpeer independencereview, and qualitythe oftherapy lifedoesn't forcure yearsthe longerdisease thanbut previouslymerely possible.delays Onethe patientinevitable, evengradual returneddecline. toGene worktherapies afteroften undergoingcarry medicalhefty retirement,price provingtags that thishealthcare therapysystems deliversstruggle real-worldto benefitsafford, beyondfurther clinicalexacerbating measurementsinequalities in access to care.

WhileThis promising,is thisthe expensivefirst successful treatment requiringto complexslow 18-hourthe brainprogression surgeryof willHuntington's remaindisease inaccessibleafter todecades mostof patientsfailed who desperately need itattempts. The results75% arereduction basedin ondisease onlyadvancement 29means patients withoutcan peermaintain review,independence and thequality therapyof doesn'tlife curefor theyears diseaselonger butthan merelypreviously delayspossible. theOne inevitable,patient gradualeven decline.returned Geneto therapieswork oftenafter carryundergoing heftymedical priceretirement, tagsproving that healthcarethis systemstherapy struggledelivers toreal-world afford,benefits furtherbeyond exacerbatingclinical inequalities in access to caremeasurements.

There'sWhile apromising, 50%this chanceexpensive thattreatment arequiring vaccinecomplex for18-hour anybrain majorsurgery neurodegenerativewill diseaseremain willinaccessible receiveto regulatorymost approvalpatients bywho Februarydesperately 2037need it. The results are based on only 29 patients without peer review, accordingand tothe therapy doesn't cure the Metaculusdisease predictionbut communitymerely delays the inevitable, gradual decline. Gene therapies often carry hefty price tags that healthcare systems struggle to afford, further exacerbating inequalities in access to care.

Metaculus Prediction

There's a 50% chance that a vaccine for any major neurodegenerative disease will receive regulatory approval by February 2037, according to the Metaculus prediction community.


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© 2025 Improve the News Foundation. All rights reserved.Version 6.15.2

© 2025 Improve the News Foundation.

All rights reserved.

Version 6.15.2