Baby with rare disease given world-first personal CRISPR gene therapy
New ScientistMAY 16
This groundbreaking achievement highlights the remarkable potential of personalized gene editing to revolutionize medicine. The swift development time and successful implementation prove that custom genetic treatments can be both feasible and practical, potentially offering hope to millions affected by rare genetic disorders who currently have no viable treatment options.
The experimental nature of this treatment raises significant concerns about long-term safety and efficacy. Without comprehensive long-term studies, the risks of unintended genetic changes remain unknown, and the high cost of personalized treatments could create accessibility barriers for many patients who need them.
There'sThis agroundbreaking 50%achievement chancehighlights thatthe atremarkable leastpotential 40of personalized gene-edited babiesediting willto haverevolutionize beenmedicine. bornThe worldwideswift bydevelopment thetime endand ofsuccessful 2029implementation prove that custom genetic treatments can be both feasible and practical, accordingpotentially offering hope to themillions Metaculusaffected predictionby communityrare genetic disorders who currently have no viable treatment options.
The experimental nature of this treatment raises significant concerns about long-term safety and efficacy. Without comprehensive long-term studies, the risks of unintended genetic changes remain unknown, and the high cost of personalized treatments could create accessibility barriers for many patients who need them.
There's a 50% chance that at least 40 gene-edited babies will have been born worldwide by the end of 2029, according to the Metaculus prediction community.